Boztug, KaanSchmidt, ManfredSchwarzer, AdrianBanerjee, Pinaki P.Avedillo Díez, InésDewey, Ricardo A.Böhm, MarieNowrouzi, AliBall, Claudia ReginaGlimm, HannoNaundorf, SonjaKühlcke, KlausBlasczyk, RainerKondratenko, IrinaMaródi, LászlóOrange, Jordan S.Kalle, Christof, vonKlein, Christoph2011-03-222011-03-222010New England Journal of Medicine. -363 : 20 (2010), p. 1918-1927. -N. Engl. J. Med. - 0028-47930028-4793http://hdl.handle.net/2437/103246Stem-cell gene therapy for the Wiskott-Aldrich syndromefolyóiratcikkopen access journal (6h embargo)http://webpac.lib.unideb.hu:8082/ebib/CorvinaWeb?action=cclfind&resultview=long&ccltext=idno+BIBFORM013545OrvostudományokKlinikai orvostudományokMassachusetts Medical Societyhttp://dx.doi.org/10.1056/NEJMoa1003548http://www.nejm.org/doi/full/10.1056/NEJMoa10035482017-12-01