Heard, Jean-MichelVrinten, CharlotteSchlander, MichaelBellettato, Cinzia Mariavan Lingen, CorineScarpa, MaurizioSzakszon, KatalinPfliegler, GyörgyKáposzta, Rita2020-01-152020-01-152020Orphanet Journal of Rare Diseases. -15 : 3 (2020), p. 1-10. -Orphanet J. Rare Dis. - 1750-1172. - 1750-11721750-1172http://hdl.handle.net/2437/278554Availability, accessibility and delivery to patients of the 28 orphan medicines approved by the European Medicine Agency for hereditary metabolic diseases in the MetabERN networkidegen nyelvű folyóiratközlemény külföldi lapbanopen access journalhttp://webpac.lib.unideb.hu:8082/ebib/CorvinaWeb?action=cclfind&resultview=long&ccltext=idno+BIBFORM082917OrvostudományokKlinikai orvostudományokhttps://ojrd.biomedcentral.com/articles/10.1186/s13023-019-1280-5http://dx.doi.org/10.1186/s13023-019-1280-52020-01-17